UCLA researchers have developed a lipid nanoparticle-based gene-editing approach capable of inserting an entire healthy gene ...

For most of his 20 years, a New Jersey man knew pain as a daily reality. Now, after a one-time CRISPR gene-editing treatment at Children's Hospital of Philadelphia, Austin Louis says he is finally ...

PORTLAND, Ore. — Doctors at OHSU’s Casey Eye Institute recently replaced defective DNA with normal DNA on a live patient. It’s part of a clinical trial called Brilliance, which is designed to bring ...

IS HOLDING A FUNDRAISER TO HELP TWO OF THEIR CHILDREN. BOTH CHILDREN HAVE A GENETIC DISORDER THAT, AMONG OTHER THINGS, CAUSES A FLOOD OF SEIZURES. AND THE ANSWER TO THE PROBLEM MAY LIE IN A GENE ...

Philadelphia and New Orleans, May 15, 2025 – In a historic medical breakthrough, a child diagnosed with a rare genetic disorder has been successfully treated with a customized CRISPR gene editing ...

The CRISPR gene-editing tool can be used to silence an important hepatitis B virus gene, a proof-of-concept in vitro study suggests. "It's the first time we've seen CRISPR editing done in a hepatitis ...

In the new approach, the pig liver remained outside the patient’s body, significantly lowering the risk of immune rejection.

Gabriella Ngang, 18, of Farmington Hills is one of just three people in Michigan to take part in a clinical trial testing a new gene-editing therapy with the potential to cure her sickle cell disease.

Congenital hearing loss refers to impaired auditory function that occurs due to genetic causes. GJB2 is the gene responsible for approximately half of all cases of hereditary hearing loss. Connexin 26 ...